How Gene Therapy Helped Conner Run
Short Wave
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From Animal Trials to Human Hope: The Journey of Gene Therapy
This chapter explores the testing process of a gene therapy for Duchenne muscular dystrophy, tracking its journey from lab experiments to animal trials with golden retrievers. It culminates in the emotional moment when the first human patient, a young boy, stands on the brink of receiving this innovative treatment, representing hope for many families.
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